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Non-syndromic bilambdoid and sagittal craniosynostosis

ORPHA:1516Malformation syndromeAutosomal recessiveNeonatal

Фенотипы (29)

Очень частый (80–99%)7
HP:0000256Macrocephaly
HP:0000268Dolichocephaly
HP:0000316Hypertelorism
HP:0000369Low-set ears
HP:0001363Craniosynostosis
HP:0002007Frontal bossing
HP:0011344Severe global developmental delay
Частый (30–79%)13
HP:0000194Open mouth
HP:0000238Hydrocephalus
HP:0000322Short philtrum
HP:0000347Micrognathia
HP:0000402Stenosis of the external auditory canal
HP:0000430Underdeveloped nasal alae
HP:0000431Wide nasal bridge
HP:0000486Strabismus
HP:0000494Downslanted palpebral fissures
HP:0001537Umbilical hernia
HP:0004209Clinodactyly of the 5th finger
HP:0004322Short stature
HP:0009891Underdeveloped supraorbital ridges
Периодический (5–29%)9
HP:0000163Abnormal oral cavity morphology
HP:0000286Epicanthus
HP:0000324Facial asymmetry
HP:0000470Short neck
HP:0000639Nystagmus
HP:0000960Sacral dimple
HP:0001052Nevus flammeus
HP:0001643Patent ductus arteriosus
HP:0002079Hypoplasia of the corpus callosum

Эпидемиология (4)

Cases/families
Worldwide
Prevalence at birth
<1 / 1 000 000
Worldwide
Point prevalence
<1 / 1 000 000
Worldwide
Prevalence at birth
<1 / 1 000 000
Spain

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы