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Thoracomelic dysplasia

ORPHA:1803DiseaseInfancy

Фенотипы (18)

Очень частый (80–99%)16
HP:0001382Joint hypermobility
HP:0000944Abnormal metaphysis morphology
HP:0001591Bell-shaped thorax
HP:0002162Low posterior hairline
HP:0002644Abnormality of pelvic girdle bone morphology
HP:0002857Genu valgum
HP:0002991Abnormal fibula morphology
HP:0003042Elbow dislocation
HP:0003307Hyperlordosis
HP:0005019Diaphyseal thickening
HP:0008873Disproportionate short-limb short stature
HP:0009826Limb undergrowth
HP:0012368Flat face
HP:0000311Round face
HP:0000773Short ribs
HP:0000774Narrow chest
Периодический (5–29%)2
HP:0000470Short neck
HP:0001288Gait disturbance

Эпидемиология (2)

Cases/families
Worldwide
Point prevalence
<1 / 1 000 000
Worldwide

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы