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Metaphyseal chondrodysplasia, Rosenberg type

ORPHA:1837DiseaseAdolescent

Фенотипы (15)

Очень частый (80–99%)5
HP:0000944Abnormal metaphysis morphology
HP:0002750Delayed skeletal maturation
HP:0003272Abnormality of the hip bone
HP:0006501Aplasia/Hypoplasia of the radius
HP:0040071Abnormal morphology of ulna
Частый (30–79%)4
HP:0002991Abnormal fibula morphology
HP:0003312Abnormal form of the vertebral bodies
HP:0004322Short stature
HP:0005916Abnormal metacarpal morphology
Периодический (5–29%)6
HP:0000164Abnormality of the dentition
HP:0000457Depressed nasal ridge
HP:0000691Microdontia
HP:0000787Nephrolithiasis
HP:0001608Abnormality of the voice
HP:0006482Abnormal dental morphology

Эпидемиология (2)

Cases/families
Worldwide
Point prevalence
<1 / 1 000 000
Worldwide

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы