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Hypertelorism-hypospadias-polysyndactyly syndrome

ORPHA:2211Malformation syndromeAutosomal recessiveNeonatal

Фенотипы (35)

Очень частый (80–99%)15
HP:0000036Abnormality of the penis
HP:0000039Epispadias
HP:0000047Hypospadias
HP:0000049Shawl scrotum
HP:0000239Large fontanelles
HP:0000248Brachycephaly
HP:0000270Delayed cranial suture closure
HP:0000316Hypertelorism
HP:0000358Posteriorly rotated ears
HP:0000369Low-set ears
HP:0000431Wide nasal bridge
HP:0000457Depressed nasal ridge
HP:0001177Preaxial hand polydactyly
HP:0005469Flat occiput
HP:0006101Finger syndactyly
Частый (30–79%)10
HP:0000048Bifid scrotum
HP:0000337Broad forehead
HP:0000343Long philtrum
HP:0000494Downslanted palpebral fissures
HP:0000501Glaucoma
HP:0000508Ptosis
HP:0000520Proptosis
HP:0000625Eyelid coloboma
HP:0010059Broad hallux phalanx
HP:0011304Broad thumb
Периодический (5–29%)10
HP:0001302Pachygyria
HP:0000960Sacral dimple
HP:0001302Pachygyria
HP:0001339Lissencephaly
HP:0002084Encephalocele
HP:0002126Polymicrogyria
HP:0002269Abnormality of neuronal migration
HP:0002536Abnormal cortical gyration
HP:0008388Abnormal toenail morphology
HP:0030769Exencephaly

Эпидемиология (2)

Cases/families
Worldwide
Point prevalence
<1 / 1 000 000
Worldwide

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы