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Müllerian duct anomalies-limb anomalies syndrome

ORPHA:2491Malformation syndromeNeonatal

Фенотипы (14)

Частый (30–79%)11
HP:0000252Microcephaly
HP:0001171Split hand
HP:0002983Micromelia
HP:0003019Abnormality of the wrist
HP:0003762Uterus didelphys
HP:0004322Short stature
HP:0005792Short humerus
HP:0006495Aplasia/Hypoplasia of the ulna
HP:0007477Abnormal dermatoglyphics
HP:0008736Hypoplasia of penis
HP:0009811Abnormality of the elbow
Периодический (5–29%)3
HP:0000486Strabismus
HP:0000821Hypothyroidism
HP:0001162Postaxial hand polydactyly

Эпидемиология (2)

Cases/families
Worldwide
Point prevalence
<1 / 1 000 000
Worldwide

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы