← Назад

Keipert syndrome

ORPHA:2662Malformation syndromeX-linked recessiveAntenatal, Infancy, Neonatal

Ассоциированные гены (1)

GPC4
glypican 4
Disease-causing germline mutation(s) in
OMIM: 300168

Фенотипы (24)

Очень частый (80–99%)11
HP:0000316Hypertelorism
HP:0000337Broad forehead
HP:0000407Sensorineural hearing impairment
HP:0000426Prominent nasal bridge
HP:0005280Depressed nasal bridge
HP:0009836Broad distal phalanx of finger
HP:0009882Short distal phalanx of finger
HP:0010059Broad hallux phalanx
HP:0010109Short hallux
HP:0010185Aplasia/Hypoplasia of the distal phalanges of the toes
HP:0011304Broad thumb
Частый (30–79%)10
HP:0000256Macrocephaly
HP:0000286Epicanthus
HP:0000327Hypoplasia of the maxilla
HP:0000508Ptosis
HP:0001609Hoarse voice
HP:0002263Exaggerated cupid's bow
HP:0004209Clinodactyly of the 5th finger
HP:0010624Aplastic/hypoplastic toenail
HP:0010804Tented upper lip vermilion
HP:0030680Abnormal cardiovascular system morphology
Периодический (5–29%)3
HP:0000708Atypical behavior
HP:0004322Short stature
HP:0100543Cognitive impairment

Эпидемиология (2)

Cases/families
Worldwide
Point prevalence
<1 / 1 000 000
Worldwide

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы