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Isolated absence of upper arm and forearm with hand present

ORPHA:294975Morphological anomalyInfancy, Neonatal

Фенотипы (18)

Очень частый (80–99%)1
HP:0009813Upper limb phocomelia
Периодический (5–29%)9
HP:0001627Abnormal heart morphology
HP:0003826Stillbirth
HP:0033127Abnormality of the musculoskeletal system
HP:0000765Abnormal thorax morphology
HP:0000925Abnormality of the vertebral column
HP:0001671Abnormal cardiac septum morphology
HP:0000271Abnormality of the face
HP:0000464Abnormality of the neck
HP:0000987Atypical scarring of skin
Очень редкий (1–4%)8
HP:0011603Congenital malformation of the great arteries
HP:0002088Abnormal lung morphology
HP:0000175Cleft palate
HP:0000104Renal agenesis
HP:0003272Abnormality of the hip bone
HP:0010442Polydactyly
HP:0001159Syndactyly
HP:0001518Small for gestational age

Эпидемиология (2)

Prevalence at birth
1-9 / 1 000 000
Worldwide
Point prevalence
Unknown
Worldwide

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы