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Radioulnar synostosis-microcephaly-scoliosis syndrome

ORPHA:3268Malformation syndromeUnknownAntenatal, Neonatal

Фенотипы (19)

Очень частый (80–99%)19
HP:0000164Abnormality of the dentition
HP:0000252Microcephaly
HP:0000286Epicanthus
HP:0000288Abnormality of the philtrum
HP:0000574Thick eyebrow
HP:0000664Synophrys
HP:0000768Pectus carinatum
HP:0000772Abnormal rib morphology
HP:0001249Intellectual disability
HP:0001263Global developmental delay
HP:0001622Premature birth
HP:0002650Scoliosis
HP:0002750Delayed skeletal maturation
HP:0002974Radioulnar synostosis
HP:0004209Clinodactyly of the 5th finger
HP:0004322Short stature
HP:0006101Finger syndactyly
HP:0007477Abnormal dermatoglyphics
HP:0009811Abnormality of the elbow

Эпидемиология (2)

Cases/families
Worldwide
Point prevalence
<1 / 1 000 000
Worldwide

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы