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Trigonocephaly-short stature-developmental delay syndrome

ORPHA:3369Malformation syndromeUnknownNo data available

Фенотипы (23)

Очень частый (80–99%)3
HP:0000243Trigonocephaly
HP:0001263Global developmental delay
HP:0004322Short stature
Частый (30–79%)20
HP:0000023Inguinal hernia
HP:0000216Broad secondary alveolar ridge
HP:0000218High palate
HP:0000237Small anterior fontanelle
HP:0000286Epicanthus
HP:0000341Narrow forehead
HP:0000431Wide nasal bridge
HP:0000601Hypotelorism
HP:0001250Seizure
HP:0001518Small for gestational age
HP:0001629Ventricular septal defect
HP:0002342Intellectual disability, moderate
HP:0005484Secondary microcephaly
HP:0005494Premature posterior fontanelle closure
HP:0005495Metopic suture patent to nasal root
HP:0005769Fifth finger distal phalanx clinodactyly
HP:0008897Postnatal growth retardation
HP:0011324Multiple suture craniosynostosis
HP:0000358Posteriorly rotated ears
HP:0000444Convex nasal ridge

Эпидемиология (2)

Cases/families
Worldwide
Point prevalence
<1 / 1 000 000
Worldwide

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы