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Familial tumoral calcinosis

ORPHA:53715DiseaseAutosomal recessiveChildhood

Фенотипы (18)

Очень частый (80–99%)4
HP:0001482Subcutaneous nodule
HP:0002653Bone pain
HP:0007470Periarticular subcutaneous nodules
HP:0100249Calcification of muscles
Частый (30–79%)3
HP:0000988Skin rash
HP:0010783Erythema
HP:0100774Hyperostosis
Периодический (5–29%)11
HP:0000121Nephrocalcinosis
HP:0000164Abnormality of the dentition
HP:0000168Abnormality of the gingiva
HP:0000174Abnormal palate morphology
HP:0000230Gingivitis
HP:0000975Hyperhidrosis
HP:0001053Hypopigmented skin patches
HP:0001609Hoarse voice
HP:0001744Splenomegaly
HP:0002240Hepatomegaly
HP:0008069Neoplasm of the skin

Эпидемиология (1)

Point prevalence
Unknown
Worldwide

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы