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Myasthenia gravis

ORPHA:589DiseaseMultigenic/multifactorial, Not applicableAll ages

Фенотипы (45)

Очень частый (80–99%)1
HP:0001324Muscle weakness
Частый (30–79%)24
HP:0000508Ptosis
HP:0000597Ophthalmoparesis
HP:0000651Diplopia
HP:0000777Abnormality of the thymus
HP:0001260Dysarthria
HP:0001283Bulbar palsy
HP:0001618Dysphonia
HP:0002015Dysphagia
HP:0002094Dyspnea
HP:0003202Skeletal muscle atrophy
HP:0003551Difficulty climbing stairs
HP:0003690Limb muscle weakness
HP:0010516Thymus hyperplasia
HP:0012378Fatigue
HP:0030006Single fiber EMG abnormality
HP:0030197Fatigable weakness of skeletal muscles
HP:0030208Acetylcholine receptor antibody positivity
HP:0030210Muscle specific kinase antibody positivity
HP:0030319Weakness of facial musculature
HP:0100614Myositis
HP:5000038Anti-titin antibody positivity
HP:5000047Anti-ryanodine receptor antibody
HP:5000048Anti-Kv1.4 antibody
HP:6000881Anti-DCC netrin 1 receptor antibody positivity
Периодический (5–29%)14
HP:0030880Raynaud phenomenon
HP:0100522Thymoma
HP:5000046Anti-Lrp4 antibody positivity
HP:0000365Hearing impairment
HP:0000836Hyperthyroidism
HP:0000872Hashimoto thyroiditis
HP:0001370Rheumatoid arthritis
HP:0002725Systemic lupus erythematosus
HP:0002878Respiratory failure
HP:0003076Glycosuria
HP:0003401Paresthesia
HP:0008207Primary adrenal insufficiency
HP:0010780Hyperacusis
HP:0012473Tongue atrophy
Очень редкий (1–4%)6
HP:0000709Psychosis
HP:0001063Acrocyanosis
HP:0001250Seizure
HP:0001878Hemolytic anemia
HP:0012115Hepatitis
HP:0012410Pure red cell aplasia

Эпидемиология (26)

Annual incidence
1-9 / 100 000
Europe
Point prevalence
1-5 / 10 000
Europe
Point prevalence
1-9 / 100 000
Worldwide
Annual incidence
1-9 / 1 000 000
United States
Point prevalence
1-5 / 10 000
Canada
Annual incidence
1-9 / 100 000
Spain
Lifetime Prevalence
1-5 / 10 000
United Kingdom
Annual incidence
1-9 / 100 000
United Kingdom
Point prevalence
1-5 / 10 000
United Kingdom
Annual incidence
1-9 / 100 000
Serbia
Point prevalence
1-5 / 10 000
United States
Point prevalence
1-5 / 10 000
Serbia
Annual incidence
1-9 / 100 000
Italy
Point prevalence
1-5 / 10 000
Austria
Annual incidence
1-9 / 100 000
Australia
Point prevalence
1-5 / 10 000
Italy
Annual incidence
1-9 / 100 000
Taiwan, Province of China
Point prevalence
1-5 / 10 000
Australia
Annual incidence
1-9 / 1 000 000
Greece
Point prevalence
1-5 / 10 000
Taiwan, Province of China
Annual incidence
1-9 / 1 000 000
Croatia
Point prevalence
1-9 / 100 000
Estonia
Point prevalence
1-9 / 100 000
Greece
Point prevalence
1-9 / 100 000
Croatia
Point prevalence
1-9 / 100 000
Egypt
Annual incidence
1-9 / 1 000 000
Worldwide

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы