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Inclusion body myositis

ORPHA:611DiseaseNot applicableAdult, Elderly

Фенотипы (14)

Очень частый (80–99%)10
HP:0002960Autoimmunity
HP:0003200Ragged-red muscle fibers
HP:0003202Skeletal muscle atrophy
HP:0003236Elevated circulating creatine kinase concentration
HP:0003457EMG abnormality
HP:0003701Proximal muscle weakness
HP:0003731Quadriceps muscle weakness
HP:0003805Rimmed vacuoles
HP:0004303Abnormal muscle fiber morphology
HP:0009071Inflammatory myopathy
Частый (30–79%)3
HP:0001315Reduced tendon reflexes
HP:0008872Feeding difficulties in infancy
HP:0034153Anti-cytosolic-5-nucleotidase-1A antibody positivity
Периодический (5–29%)1
HP:0003326Myalgia

Эпидемиология (7)

Point prevalence
1-9 / 1 000 000
Europe
Annual incidence
1-9 / 1 000 000
Sweden
Point prevalence
1-9 / 1 000 000
Netherlands
Point prevalence
1-9 / 100 000
Australia
Point prevalence
1-9 / 100 000
United States
Point prevalence
1-9 / 1 000 000
Turkey
Point prevalence
1-9 / 100 000
Sweden

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы