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Morgagni-Stewart-Morel syndrome

ORPHA:77296Malformation syndromeAutosomal dominant, X-linked recessiveAdult

Фенотипы (30)

Облигатный (100%)1
HP:0004438Hyperostosis frontalis interna
Очень частый (80–99%)6
HP:0000707Abnormality of the nervous system
HP:0000708Atypical behavior
HP:0000818Abnormality of the endocrine system
HP:0001513Obesity
HP:0002315Headache
HP:0032245Abnormal metabolism
Частый (30–79%)4
HP:0000819Diabetes mellitus
HP:0001007Hirsutism
HP:0002076Migraine
HP:0002120Cerebral cortical atrophy
Периодический (5–29%)19
HP:0000716Depression
HP:0000725Psychotic episodes
HP:0000820Abnormality of the thyroid gland
HP:0000821Hypothyroidism
HP:0000822Hypertension
HP:0000939Osteoporosis
HP:0001061Acne
HP:0001250Seizure
HP:0001348Brisk reflexes
HP:0002149Hyperuricemia
HP:0002310Orofacial dyskinesia
HP:0002321Vertigo
HP:0002345Action tremor
HP:0002354Memory impairment
HP:0002758Osteoarthritis
HP:0003124Hypercholesterolemia
HP:0012444Brain atrophy
HP:0031589Suicidal ideation
HP:0100543Cognitive impairment

Эпидемиология (1)

Point prevalence
Unknown
Worldwide

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы