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Acquired generalized lipodystrophy

ORPHA:79086DiseaseNot applicableAll ages

Фенотипы (28)

Облигатный (100%)1
HP:0009064Generalized lipodystrophy
Очень частый (80–99%)2
HP:0000842Hyperinsulinemia
HP:0000855Insulin resistance
Частый (30–79%)8
HP:0000831Insulin-resistant diabetes mellitus
HP:0001397Hepatic steatosis
HP:0001638Cardiomyopathy
HP:0002960Autoimmunity
HP:0003119Abnormal circulating lipid concentration
HP:0003707Calf muscle pseudohypertrophy
HP:0005328Progeroid facial appearance
HP:0011025Abnormality of cardiovascular system physiology
Периодический (5–29%)14
HP:0000093Proteinuria
HP:0000147Polycystic ovaries
HP:0000822Hypertension
HP:0000956Acanthosis nigricans
HP:0001394Cirrhosis
HP:0001735Acute pancreatitis
HP:0002155Hypertriglyceridemia
HP:0002230Generalized hirsutism
HP:0002240Hepatomegaly
HP:0003198Myopathy
HP:0005339Abnormality of complement system
HP:0005616Accelerated skeletal maturation
HP:0007440Generalized hyperpigmentation
HP:0012490Panniculitis
Очень редкий (1–4%)3
HP:0002665Lymphoma
HP:0009592Astrocytoma
HP:0012064Unicameral bone cyst

Эпидемиология (2)

Point prevalence
Unknown
Worldwide
Point prevalence
1-9 / 100 000
Europe

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы