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Myelodysplastic neoplasm with increased blasts

ORPHA:86839DiseaseNot applicableAdult

Фенотипы (22)

Очень частый (80–99%)2
HP:0010972Anemia of inadequate production
HP:0012378Fatigue
Частый (30–79%)4
HP:0001017Anemic pallor
HP:0001945Fever
HP:0001962Palpitations
HP:0002875Exertional dyspnea
Периодический (5–29%)16
HP:0000573Retinal hemorrhage
HP:0001873Thrombocytopenia
HP:0001892Abnormal bleeding
HP:0001974Leukocytosis
HP:0002653Bone pain
HP:0004808Acute myeloid leukemia
HP:0005528Bone marrow hypocellularity
HP:0005561Abnormality of bone marrow cell morphology
HP:0010741Pedal edema
HP:0010876Abnormal circulating protein level
HP:0012116Abnormal albumin level
HP:0012136Dysplastic granulopoesis
HP:0012148Multiple lineage myelodysplasia
HP:0012150Single lineage myelodysplasia
HP:0025065Abnormal mean corpuscular volume
HP:0031035Chronic infection

Эпидемиология (2)

Point prevalence
Unknown
Worldwide
Annual incidence
1-9 / 1 000 000
Europe

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы