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PAGOD syndrome

ORPHA:991Malformation syndromeNot applicableNeonatal

Фенотипы (31)

Очень частый (80–99%)5
HP:0000008Abnormal morphology of female internal genitalia
HP:0002089Pulmonary hypoplasia
HP:0004414Abnormality of the pulmonary artery
HP:0004971Pulmonary artery hypoplasia
HP:0030680Abnormal cardiovascular system morphology
Частый (30–79%)11
HP:0000003Multicystic kidney dysplasia
HP:0000035Abnormal testis morphology
HP:0000062Ambiguous genitalia
HP:0000130Abnormality of the uterus
HP:0000776Congenital diaphragmatic hernia
HP:0001522Death in infancy
HP:0001539Omphalocele
HP:0004383Hypoplastic left heart
HP:0008633Agonadism
HP:0008678Renal hypoplasia/aplasia
HP:0010458Female pseudohermaphroditism
Периодический (5–29%)15
HP:0000252Microcephaly
HP:0000648Optic atrophy
HP:0000772Abnormal rib morphology
HP:0000889Abnormality of the clavicle
HP:0001645Sudden cardiac death
HP:0001679Abnormal aortic morphology
HP:0001696Situs inversus totalis
HP:0001743Abnormality of the spleen
HP:0002084Encephalocele
HP:0002269Abnormality of neuronal migration
HP:0002414Spina bifida
HP:0002435Meningocele
HP:0004322Short stature
HP:0011675Arrhythmia
HP:0100555Asymmetric growth

Эпидемиология (2)

Cases/families
Worldwide
Point prevalence
<1 / 1 000 000
Worldwide

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы