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Familial pancreatic carcinoma

ORPHA:1333DiseaseAutosomal dominant, Multigenic/multifactorialAdult

Ассоциированные гены (9)

BRCA1
BRCA1 DNA repair associated
Major susceptibility factor in
OMIM: 113705
BRCA2
BRCA2 DNA repair associated
Major susceptibility factor in
OMIM: 600185
CDKN2A
cyclin dependent kinase inhibitor 2A
Major susceptibility factor in
OMIM: 600160
SMAD4
SMAD family member 4
Major susceptibility factor in
OMIM: 600993
TP53
tumor protein p53
Major susceptibility factor in
OMIM: 191170
KRAS
KRAS proto-oncogene, GTPase
Major susceptibility factor in
OMIM: 190070
PALB2
partner and localizer of BRCA2
Major susceptibility factor in
OMIM: 610355
PALLD
palladin, cytoskeletal associated protein
Major susceptibility factor in
OMIM: 608092
RABL3
RAB, member of RAS oncogene family like 3
Disease-causing germline mutation(s) in
OMIM: 618542

Фенотипы (24)

Облигатный (100%)1
HP:0006725Pancreatic adenocarcinoma
Очень частый (80–99%)7
HP:0001738Exocrine pancreatic insufficiency
HP:0001824Weight loss
HP:0002027Abdominal pain
HP:0002039Anorexia
HP:0003418Back pain
HP:0004396Poor appetite
HP:0012432Chronic fatigue
Частый (30–79%)5
HP:0000952Jaundice
HP:0002716Lymphadenopathy
HP:0004389Intestinal pseudo-obstruction
HP:0005249Functional intestinal obstruction
HP:0012334Extrahepatic cholestasis
Периодический (5–29%)11
HP:0000819Diabetes mellitus
HP:0001433Hepatosplenomegaly
HP:0002017Nausea and vomiting
HP:0002254Intermittent diarrhea
HP:0002861Melanoma
HP:0002896Neoplasm of the liver
HP:0002910Elevated circulating hepatic transaminase concentration
HP:0003002Breast carcinoma
HP:0003003Colon cancer
HP:0025318Ovarian carcinoma
HP:0100592Peritoneal abscess

Эпидемиология (1)

Point prevalence
1-9 / 1 000 000
Europe

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы