← Назад

CHILD syndrome

ORPHA:139DiseaseX-linked dominantAntenatal, Infancy, Neonatal

Ассоциированные гены (1)

NSDHL
NAD(P) dependent 3-beta-hydroxysteroid dehydrogenase NSDHL
Disease-causing germline mutation(s) in
OMIM: 300275

Фенотипы (23)

Очень частый (80–99%)1
HP:0010655Epiphyseal stippling
Частый (30–79%)9
HP:0000962Hyperkeratosis
HP:0001036Parakeratosis
HP:0007431Congenital ichthyosiform erythroderma
HP:0008394Congenital onychodystrophy
HP:0010049Short metacarpal
HP:0025092Epidermal acanthosis
HP:0031517Verruciform xanthoma
HP:0045060Aplasia/hypoplasia involving bones of the extremities
HP:0100803Abnormality of the periungual region
Периодический (5–29%)9
HP:0012165Oligodactyly
HP:0001627Abnormal heart morphology
HP:0002011Morphological central nervous system abnormality
HP:0002089Pulmonary hypoplasia
HP:0002650Scoliosis
HP:0002828Multiple joint contractures
HP:0003651Foam cells
HP:0004552Scarring alopecia of scalp
HP:0009827Amelia
Очень редкий (1–4%)4
HP:0000104Renal agenesis
HP:0000126Hydronephrosis
HP:0001159Syndactyly
HP:0010442Polydactyly

Эпидемиология (2)

Cases/families
Worldwide
Point prevalence
<1 / 1 000 000
Worldwide

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы