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Immunodeficiency due to a classical component pathway complement deficiency

ORPHA:169147DiseaseAutosomal recessive

Ассоциированные гены (8)

C2
complement C2
Disease-causing germline mutation(s) in
OMIM: 613927
C4A
complement C4A (Chido/Rodgers blood group)
Disease-causing germline mutation(s) in
OMIM: 120810
C4B
complement C4B (Chido/Rodgers blood group)
Disease-causing germline mutation(s) in
OMIM: 120820
C1QA
complement C1q A chain
Disease-causing germline mutation(s) in
OMIM: 120550
C1QB
complement C1q B chain
Disease-causing germline mutation(s) in
OMIM: 120570
C1QC
complement C1q C chain
Disease-causing germline mutation(s) in
OMIM: 120575
C1S
complement C1s
Disease-causing germline mutation(s) in
OMIM: 120580
C1R
complement C1r
Disease-causing germline mutation(s) in
OMIM: 613785

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы