← Назад

XY type gonadal dysgenesis-associated anomalies syndrome

ORPHA:1770Malformation syndromeAutosomal recessiveNeonatal

Ассоциированные гены (1)

PPP2R3C
protein phosphatase 2 regulatory subunit B''gamma
Disease-causing germline mutation(s) in
OMIM: 615902

Фенотипы (26)

Очень частый (80–99%)16
HP:0000069Abnormality of the ureter
HP:0000133Gonadal dysgenesis
HP:0000147Polycystic ovaries
HP:0000413Atresia of the external auditory canal
HP:0001156Brachydactyly
HP:0001176Large hands
HP:0001256Intellectual disability, mild
HP:0001537Umbilical hernia
HP:0001629Ventricular septal defect
HP:0002750Delayed skeletal maturation
HP:0004422Biparietal narrowing
HP:0004467Preauricular pit
HP:0007598Bilateral single transverse palmar creases
HP:0010720Abnormal hair pattern
HP:0011304Broad thumb
HP:0011342Mild global developmental delay
Частый (30–79%)10
HP:0000175Cleft palate
HP:0000286Epicanthus
HP:0000288Abnormality of the philtrum
HP:0000494Downslanted palpebral fissures
HP:0002000Short columella
HP:0004322Short stature
HP:0008551Microtia
HP:0008678Renal hypoplasia/aplasia
HP:0100335Non-midline cleft of the upper lip
HP:0000358Posteriorly rotated ears

Эпидемиология (2)

Cases/families
Worldwide
Point prevalence
<1 / 1 000 000
Worldwide

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы