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Cherubism

ORPHA:184Malformation syndromeAutosomal dominant, Autosomal recessive, Not applicableChildhood

Ассоциированные гены (1)

SH3BP2
SH3 domain binding protein 2
Disease-causing germline mutation(s) in
OMIM: 602104

Фенотипы (15)

Очень частый (80–99%)4
HP:0000277Abnormality of the mandible
HP:0000293Full cheeks
HP:0012062Bone cyst
HP:0012802Broad jaw
Частый (30–79%)3
HP:0000164Abnormality of the dentition
HP:0000677Oligodontia
HP:0006482Abnormal dental morphology
Периодический (5–29%)8
HP:0000505Visual impairment
HP:0000520Proptosis
HP:0000529Progressive visual loss
HP:0000648Optic atrophy
HP:0001608Abnormality of the voice
HP:0002781Upper airway obstruction
HP:0002870Obstructive sleep apnea
HP:0008872Feeding difficulties in infancy

Эпидемиология (2)

Point prevalence
<1 / 1 000 000
Worldwide
Cases/families
Worldwide

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы