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Primary biliary cholangitis

ORPHA:186DiseaseMultigenic/multifactorial, UnknownAdolescent, Adult, Elderly

Ассоциированные гены (8)

IL12RB1
interleukin 12 receptor subunit beta 1
Major susceptibility factor in
OMIM: 601604
SPIB
Spi-B transcription factor
Major susceptibility factor in
OMIM: 606802
IL12A
interleukin 12A
Major susceptibility factor in
OMIM: 161560
IRF5
interferon regulatory factor 5
Major susceptibility factor in
OMIM: 607218
TNPO3
transportin 3
Major susceptibility factor in
OMIM: 610032
MMEL1
membrane metalloendopeptidase like 1
Major susceptibility factor in
OMIM: 618104
POU2AF1
POU class 2 homeobox associating factor 1
Major susceptibility factor in
OMIM: 601206
TNFSF15
TNF superfamily member 15
Major susceptibility factor in
OMIM: 604052

Фенотипы (41)

Очень частый (80–99%)6
HP:0000953Hyperpigmentation of the skin
HP:0001394Cirrhosis
HP:0002613Biliary cirrhosis
HP:0002908Conjugated hyperbilirubinemia
HP:0011971Dermatographic urticaria
HP:0030167Antimitochondrial antibody positivity
Частый (30–79%)20
HP:0000820Abnormality of the thyroid gland
HP:0000952Jaundice
HP:0000989Pruritus
HP:0001114Xanthelasma
HP:0001278Orthostatic hypotension
HP:0001395Hepatic fibrosis
HP:0001399Hepatic failure
HP:0001402Hepatocellular carcinoma
HP:0001409Portal hypertension
HP:0002240Hepatomegaly
HP:0002841Recurrent fungal infections
HP:0002960Autoimmunity
HP:0003119Abnormal circulating lipid concentration
HP:0003124Hypercholesterolemia
HP:0003155Elevated circulating alkaline phosphatase concentration
HP:0003493Antinuclear antibody positivity
HP:0003496Increased circulating IgM level
HP:0011040Abnormality of the intrahepatic bile duct
HP:0012203Onychomycosis
HP:0030948Elevated gamma-glutamyltransferase level
Периодический (5–29%)14
HP:0000939Osteoporosis
HP:0001262Excessive daytime somnolence
HP:0001541Ascites
HP:0001744Splenomegaly
HP:0002040Esophageal varix
HP:0002360Sleep abnormality
HP:0002480Hepatic encephalopathy
HP:0002570Steatorrhea
HP:0002608Celiac disease
HP:0003073Hypoalbuminemia
HP:0003261Increased circulating IgA level
HP:0003270Abdominal distention
HP:0012115Hepatitis
HP:0012378Fatigue
Очень редкий (1–4%)1
HP:0004386Gastrointestinal inflammation

Эпидемиология (28)

Annual incidence
1-9 / 100 000
Europe
Point prevalence
1-5 / 10 000
Worldwide
Annual incidence
1-9 / 100 000
Worldwide
Point prevalence
1-5 / 10 000
Europe
Annual incidence
1-9 / 1 000 000
France
Annual incidence
1-9 / 100 000
Spain
Point prevalence
1-5 / 10 000
Spain
Annual incidence
1-9 / 100 000
Iceland
Point prevalence
1-5 / 10 000
Iceland
Annual incidence
1-9 / 100 000
Netherlands
Point prevalence
1-5 / 10 000
Netherlands
Annual incidence
1-9 / 100 000
Denmark
Point prevalence
1-5 / 10 000
Denmark
Annual incidence
1-9 / 100 000
Finland
Point prevalence
1-5 / 10 000
Finland
Point prevalence
1-5 / 10 000
United Kingdom
Annual incidence
1-9 / 100 000
United States
Point prevalence
1-5 / 10 000
United States
Annual incidence
1-9 / 100 000
Canada
Point prevalence
1-5 / 10 000
Canada
Point prevalence
1-9 / 100 000
Australia
Point prevalence
1-9 / 100 000
Israel
Point prevalence
1-9 / 100 000
China
Annual incidence
1-9 / 100 000
Brunei Darussalam
Point prevalence
1-9 / 100 000
Brunei Darussalam
Point prevalence
1-5 / 10 000
Greece
Annual incidence
1-9 / 100 000
Greece
Annual incidence
1-9 / 100 000
United Kingdom

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы