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Self-limited neonatal epilepsy

ORPHA:1949DiseaseAutosomal dominantNeonatal

Ассоциированные гены (2)

KCNQ2
potassium voltage-gated channel subfamily Q member 2
Disease-causing germline mutation(s) in
OMIM: 602235
KCNQ3
potassium voltage-gated channel subfamily Q member 3
Disease-causing germline mutation(s) in
OMIM: 602232

Фенотипы (17)

Очень частый (80–99%)5
HP:0002266Focal clonic seizure
HP:0007359Focal-onset seizure
HP:0011167Focal tonic seizure
HP:0011188Focal EEG discharges with secondary generalization
HP:0032807Neonatal seizure
Частый (30–79%)6
HP:0002104Apnea
HP:0002169Clonus
HP:0010818Generalized tonic seizure
HP:0011154Focal autonomic seizure
HP:0032556Circumoral cyanosis
HP:0045084Limb myoclonus
Периодический (5–29%)4
HP:0002020Gastroesophageal reflux
HP:0008936Axial hypotonia
HP:0011171Simple febrile seizures
HP:0011468Facial tics
Очень редкий (1–4%)2
HP:0002133Status epilepticus
HP:0031535Increased theta frequency activity in EEG

Эпидемиология (2)

Cases/families
Worldwide
Point prevalence
Unknown
Worldwide

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы