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Hartsfield syndrome

ORPHA:2117Malformation syndromeAutosomal dominant, Autosomal recessiveAntenatal

Ассоциированные гены (1)

FGFR1
fibroblast growth factor receptor 1
Disease-causing germline mutation(s) (loss of function) in
OMIM: 136350

Фенотипы (17)

Очень частый (80–99%)15
HP:0000175Cleft palate
HP:0000316Hypertelorism
HP:0000494Downslanted palpebral fissures
HP:0000506Telecanthus
HP:0000508Ptosis
HP:0000568Microphthalmia
HP:0001363Craniosynostosis
HP:0001511Intrauterine growth retardation
HP:0002084Encephalocele
HP:0002093Respiratory insufficiency
HP:0005280Depressed nasal bridge
HP:0006870Lobar holoprosencephaly
HP:0007370Aplasia/Hypoplasia of the corpus callosum
HP:0100335Non-midline cleft of the upper lip
HP:0000358Posteriorly rotated ears
Частый (30–79%)2
HP:0001171Split hand
HP:0006501Aplasia/Hypoplasia of the radius

Эпидемиология (2)

Cases/families
Worldwide
Point prevalence
<1 / 1 000 000
Worldwide

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы