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46,XX ovotesticular difference of sex development

ORPHA:2138Malformation syndromeAutosomal dominant, Autosomal recessiveAdolescent, Antenatal, Neonatal

Ассоциированные гены (3)

SOX9
SRY-box transcription factor 9
Disease-causing germline mutation(s) in
OMIM: 608160
SRY
sex determining region Y
Disease-causing germline mutation(s) in
OMIM: 480000
NR5A1
nuclear receptor subfamily 5 group A member 1
Disease-causing germline mutation(s) (loss of function) in
OMIM: 184757

Фенотипы (14)

Очень частый (80–99%)14
HP:0000008Abnormal morphology of female internal genitalia
HP:0000022Abnormality of male internal genitalia
HP:0000028Cryptorchidism
HP:0000046Small scrotum
HP:0000047Hypospadias
HP:0000048Bifid scrotum
HP:0000062Ambiguous genitalia
HP:0000130Abnormality of the uterus
HP:0000144Decreased fertility
HP:0000147Polycystic ovaries
HP:0008736Hypoplasia of penis
HP:0010459True hermaphroditism
HP:0012856Abnormal scrotal rugation
HP:0100779Urogenital sinus anomaly

Эпидемиология (3)

Cases/families
Worldwide
Prevalence at birth
1-9 / 100 000
Worldwide
Point prevalence
1-9 / 100 000
Europe

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы