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Hypodontia-dysplasia of nails syndrome

ORPHA:2228Malformation syndromeAutosomal dominantChildhood

Ассоциированные гены (1)

MSX1
msh homeobox 1
Disease-causing germline mutation(s) in
OMIM: 142983

Фенотипы (16)

Очень частый (80–99%)13
HP:0000164Abnormality of the dentition
HP:0000668Hypodontia
HP:0000684Delayed eruption of teeth
HP:0000698Conical tooth
HP:0001231Abnormal fingernail morphology
HP:0001597Abnormality of the nail
HP:0001800Hypoplastic toenails
HP:0001804Hypoplastic fingernail
HP:0001808Fragile nails
HP:0006349Agenesis of permanent teeth
HP:0006482Abnormal dental morphology
HP:0008402Ridged fingernail
HP:0012746Thin toenail
Частый (30–79%)2
HP:0000232Everted lower lip vermilion
HP:0002213Fine hair
Периодический (5–29%)1
HP:0000147Polycystic ovaries

Эпидемиология (1)

Point prevalence
Unknown
Worldwide

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы