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Prune belly syndrome

ORPHA:2970Malformation syndromeAutosomal dominant, Not applicable, X-linked recessiveAntenatal, Neonatal

Ассоциированные гены (1)

CHRM3
cholinergic receptor muscarinic 3
Disease-causing germline mutation(s) (loss of function) in
OMIM: 118494

Фенотипы (34)

Очень частый (80–99%)9
HP:0000014Abnormality of the bladder
HP:0000028Cryptorchidism
HP:0000069Abnormality of the ureter
HP:0000072Hydroureter
HP:0000076Vesicoureteral reflux
HP:0000144Decreased fertility
HP:0005199Aplasia of the abdominal wall musculature
HP:0006703Aplasia/Hypoplasia of the lungs
HP:0010957Congenital posterior urethral valve
Частый (30–79%)8
HP:0000003Multicystic kidney dysplasia
HP:0000010Recurrent urinary tract infections
HP:0000083Renal insufficiency
HP:0000772Abnormal rib morphology
HP:0001562Oligohydramnios
HP:0002019Constipation
HP:0002205Recurrent respiratory infections
HP:0008734Decreased testicular size
Периодический (5–29%)17
HP:0000130Abnormality of the uterus
HP:0000767Pectus excavatum
HP:0001374Congenital hip dislocation
HP:0001508Failure to thrive
HP:0001629Ventricular septal defect
HP:0001631Atrial septal defect
HP:0001636Tetralogy of Fallot
HP:0001643Patent ductus arteriosus
HP:0001762Talipes equinovarus
HP:0002023Anal atresia
HP:0002566Intestinal malrotation
HP:0002580Volvulus
HP:0002650Scoliosis
HP:0003422Vertebral segmentation defect
HP:0011100Intestinal atresia
HP:0100543Cognitive impairment
HP:0100779Urogenital sinus anomaly

Эпидемиология (5)

Prevalence at birth
1-9 / 100 000
Italy
Prevalence at birth
1-9 / 1 000 000
United Kingdom
Prevalence at birth
1-9 / 100 000
Canada
Prevalence at birth
1-9 / 100 000
United States
Point prevalence
Unknown
Worldwide

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы