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Autosomal systemic lupus erythematosus

ORPHA:300345DiseaseAutosomal dominant, Autosomal recessiveChildhood

Ассоциированные гены (5)

C1QA
complement C1q A chain
Major susceptibility factor in
OMIM: 120550
C4A
complement C4A (Chido/Rodgers blood group)
Major susceptibility factor in
OMIM: 120810
DNASE1L3
deoxyribonuclease 1L3
Disease-causing germline mutation(s) (loss of function) in
OMIM: 602244
C1R
complement C1r
Disease-causing germline mutation(s) (loss of function) in
OMIM: 613785
DNASE1
deoxyribonuclease 1
Disease-causing germline mutation(s) in
OMIM: 125505

Эпидемиология (2)

Cases/families
Worldwide
Point prevalence
<1 / 1 000 000
Worldwide

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы