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Inherited epidermodysplasia verruciformis

ORPHA:302DiseaseAutosomal recessiveAll ages

Ассоциированные гены (4)

TMC6
transmembrane channel like 6
Disease-causing germline mutation(s) (loss of function) in
OMIM: 605828
TMC8
transmembrane channel like 8
Disease-causing germline mutation(s) (loss of function) in
OMIM: 605829
IL7
interleukin 7
Disease-causing germline mutation(s) in
OMIM: 146660
CIB1
calcium and integrin binding 1
Disease-causing germline mutation(s) in
OMIM: 602293

Фенотипы (11)

Очень частый (80–99%)7
HP:0001051Seborrheic dermatitis
HP:0001581Recurrent skin infections
HP:0002715Abnormality of the immune system
HP:0200034Papule
HP:0200035Skin plaque
HP:0200039Pustule
HP:0200043Verrucae
Частый (30–79%)2
HP:0001053Hypopigmented skin patches
HP:0007565Multiple cafe-au-lait spots
Периодический (5–29%)2
HP:0002860Squamous cell carcinoma
HP:0100585Telangiectasia of the skin

Эпидемиология (2)

Cases/families
Worldwide
Point prevalence
<1 / 1 000 000
Worldwide

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы