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Congenital factor II deficiency

ORPHA:325DiseaseAutosomal recessiveAll ages

Ассоциированные гены (1)

F2
coagulation factor II, thrombin
Disease-causing germline mutation(s) in
OMIM: 176930

Фенотипы (21)

Очень частый (80–99%)3
HP:0003645Prolonged partial thromboplastin time
HP:0008151Prolonged prothrombin time
HP:0040250Reduced prothrombin antigen
Частый (30–79%)4
HP:0000421Epistaxis
HP:0001892Abnormal bleeding
HP:0002170Intracranial hemorrhage
HP:0005261Joint hemorrhage
Периодический (5–29%)12
HP:0000132Menorrhagia
HP:0001903Anemia
HP:0002907Microscopic hematuria
HP:0006298Prolonged bleeding after dental extraction
HP:0011884Abnormal umbilical stump bleeding
HP:0011890Prolonged bleeding following procedure
HP:0011891Post-partum hemorrhage
HP:0012233Intramuscular hematoma
HP:0012541Cephalohematoma
HP:0030137Prolonged bleeding following circumcision
HP:0030138Excessive bleeding from superficial cuts
HP:0030140Oral cavity bleeding
Исключён (0%)2
HP:0004420Arterial thrombosis
HP:0004936Venous thrombosis

Эпидемиология (1)

Point prevalence
<1 / 1 000 000
Europe

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы