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Congenital factor XIII deficiency

ORPHA:331DiseaseAutosomal recessive, Not applicableAll ages

Ассоциированные гены (2)

F13A1
coagulation factor XIII A chain
Disease-causing germline mutation(s) in
OMIM: 134570
F13B
coagulation factor XIII B chain
Disease-causing germline mutation(s) in
OMIM: 134580

Фенотипы (26)

Очень частый (80–99%)3
HP:0008357Reduced factor XIII activity
HP:0011884Abnormal umbilical stump bleeding
HP:0030657Umbilical cord hematoma
Частый (30–79%)7
HP:0000978Bruising susceptibility
HP:0001342Cerebral hemorrhage
HP:0001933Subcutaneous hemorrhage
HP:0005261Joint hemorrhage
HP:0007420Spontaneous hematomas
HP:0012233Intramuscular hematoma
HP:0030140Oral cavity bleeding
Периодический (5–29%)13
HP:0000132Menorrhagia
HP:0000225Gingival bleeding
HP:0000421Epistaxis
HP:0001058Poor wound healing
HP:0001934Persistent bleeding after trauma
HP:0004846Prolonged bleeding after surgery
HP:0006298Prolonged bleeding after dental extraction
HP:0011889Bleeding with minor or no trauma
HP:0011891Post-partum hemorrhage
HP:0030137Prolonged bleeding following circumcision
HP:0031364Ecchymosis
HP:0040232Delayed onset bleeding
HP:0200067Recurrent spontaneous abortion
Очень редкий (1–4%)3
HP:0001399Hepatic failure
HP:0002037Inflammation of the large intestine
HP:0012324Myeloid leukemia

Эпидемиология (2)

Annual incidence
<1 / 1 000 000
Europe
Point prevalence
<1 / 1 000 000
Europe

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы