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Non-syndromic bicoronal craniosynostosis

ORPHA:35099Morphological anomalyAutosomal dominant, Not applicableInfancy, Neonatal

Ассоциированные гены (4)

FGFR3
fibroblast growth factor receptor 3
Disease-causing germline mutation(s) in
OMIM: 134934
ZIC1
Zic family zinc finger 1
Disease-causing germline mutation(s) (gain of function) in
OMIM: 600470
TCF12
transcription factor 12
Disease-causing germline mutation(s) (loss of function) in
OMIM: 600480
TWIST1
twist family bHLH transcription factor 1
Disease-causing germline mutation(s) in
OMIM: 601622

Фенотипы (11)

Очень частый (80–99%)2
HP:0000248Brachycephaly
HP:0000337Broad forehead
Частый (30–79%)4
HP:0000365Hearing impairment
HP:0000520Proptosis
HP:0002516Increased intracranial pressure
HP:0009891Underdeveloped supraorbital ridges
Периодический (5–29%)5
HP:0000316Hypertelorism
HP:0001156Brachydactyly
HP:0001249Intellectual disability
HP:0009701Metacarpal synostosis
HP:0011800Midface retrusion

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы