← Назад

Acute encephalopathy with biphasic seizures and late reduced diffusion

ORPHA:363549DiseaseInfancy, Neonatal

Ассоциированные гены (1)

ADORA2A
adenosine A2a receptor
Major susceptibility factor in
OMIM: 102776

Фенотипы (12)

Очень частый (80–99%)1
HP:0002069Bilateral tonic-clonic seizure
Частый (30–79%)8
HP:0007103Hypointensity of cerebral white matter on MRI
HP:0007185Loss of consciousness
HP:0011172Complex febrile seizure
HP:0012705Abnormal metabolic brain imaging by MRS
HP:0031691Severe viral infection
HP:0032308Increased circulating procalcitonin concentration
HP:0032894Seizure precipitated by febrile infection
HP:0033349Seizure cluster
Периодический (5–29%)2
HP:0007738Uncontrolled eye movements
HP:0031475Status epilepticus without prominent motor symptoms
Очень редкий (1–4%)1
HP:0011665Takotsubo cardiomyopathy

Эпидемиология (2)

Cases/families
Worldwide
Point prevalence
<1 / 1 000 000
Worldwide

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы