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Uveal melanoma

ORPHA:39044DiseaseNot applicableAdult

Ассоциированные гены (6)

CYSLTR2
cysteinyl leukotriene receptor 2
Disease-causing somatic mutation(s) in
OMIM: 605666
BAP1
BRCA1 associated deubiquitinase 1
Disease-causing germline mutation(s) in
OMIM: 603089
BAP1
BRCA1 associated deubiquitinase 1
Disease-causing somatic mutation(s) in
OMIM: 603089
GNAQ
G protein subunit alpha q
Disease-causing somatic mutation(s) in
OMIM: 600998
GNA11
G protein subunit alpha 11
Disease-causing somatic mutation(s) in
OMIM: 139313
SF3B1
splicing factor 3b subunit 1
Biomarker tested in
OMIM: 605590

Фенотипы (17)

Очень частый (80–99%)3
HP:0000572Visual loss
HP:0001098Abnormal fundus morphology
HP:0012054Choroidal melanoma
Частый (30–79%)3
HP:0000541Retinal detachment
HP:0011524Iris melanoma
HP:0012055Ciliary body melanoma
Периодический (5–29%)9
HP:0000539Abnormality of refraction
HP:0007902Vitreous hemorrhage
HP:0007906Ocular hypertension
HP:0008494Inferior lens subluxation
HP:0010920Zonular cataract
HP:0011499Mydriasis
HP:0012508Metamorphopsia
HP:0030786Photopsia
HP:0030800Abnormal visual accommodation
Очень редкий (1–4%)2
HP:0100533Inflammatory abnormality of the eye
HP:0200026Ocular pain

Эпидемиология (4)

Annual incidence
1-9 / 1 000 000
Europe
Point prevalence
1-9 / 100 000
Europe
Lifetime Prevalence
1-9 / 100 000
Europe
Annual incidence
<1 / 1 000 000
Africa

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы