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Hereditary fructose intolerance

ORPHA:469DiseaseAutosomal recessiveAll ages

Ассоциированные гены (1)

ALDOB
aldolase, fructose-bisphosphate B
Disease-causing germline mutation(s) in
OMIM: 612724

Фенотипы (24)

Очень частый (80–99%)2
HP:0002027Abdominal pain
HP:0012545Reduced aldolase level
Частый (30–79%)3
HP:0001510Growth delay
HP:0002014Diarrhea
HP:0002018Nausea
Периодический (5–29%)15
HP:0000083Renal insufficiency
HP:0000952Jaundice
HP:0001069Episodic hyperhidrosis
HP:0001942Metabolic acidosis
HP:0002013Vomiting
HP:0002019Constipation
HP:0002148Hypophosphatemia
HP:0002149Hyperuricemia
HP:0002240Hepatomegaly
HP:0002918Hypermagnesemia
HP:0003256Abnormality of the coagulation cascade
HP:0003270Abdominal distention
HP:0012051Reactive hypoglycemia
HP:0012622Chronic kidney disease
HP:0100626Chronic hepatic failure
Очень редкий (1–4%)4
HP:0000518Cataract
HP:0001250Seizure
HP:0001254Lethargy
HP:0001259Coma

Эпидемиология (13)

Point prevalence
1-9 / 100 000
Europe
Prevalence at birth
1-9 / 100 000
Switzerland
Point prevalence
1-9 / 100 000
Switzerland
Prevalence at birth
1-9 / 100 000
United Kingdom
Point prevalence
1-9 / 100 000
United Kingdom
Prevalence at birth
1-9 / 100 000
Germany
Point prevalence
1-9 / 100 000
Germany
Prevalence at birth
1-9 / 100 000
Poland
Point prevalence
1-9 / 100 000
Poland
Point prevalence
1-9 / 100 000
Finland
Point prevalence
1-9 / 1 000 000
United States
Point prevalence
1-9 / 1 000 000
Specific population
Point prevalence
1-9 / 1 000 000
China

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы