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Congenital short QT syndrome

ORPHA:51083DiseaseAutosomal dominantAll ages

Ассоциированные гены (5)

SLC4A3
solute carrier family 4 member 3
Disease-causing germline mutation(s) (loss of function) in
OMIM: 106195
KCNJ2
potassium inwardly rectifying channel subfamily J member 2
Disease-causing germline mutation(s) (gain of function) in
OMIM: 600681
KCNH2
potassium voltage-gated channel subfamily H member 2
Disease-causing germline mutation(s) (gain of function) in
OMIM: 152427
KCNQ1
potassium voltage-gated channel subfamily Q member 1
Disease-causing germline mutation(s) (gain of function) in
OMIM: 607542
CACNA2D1
calcium voltage-gated channel auxiliary subunit alpha2delta 1
Disease-causing germline mutation(s) (loss of function) in
OMIM: 114204

Фенотипы (9)

Облигатный (100%)1
HP:0012232Shortened QT interval
Очень частый (80–99%)1
HP:0001662Bradycardia
Частый (30–79%)2
HP:0001962Palpitations
HP:0005110Atrial fibrillation
Периодический (5–29%)5
HP:0001279Syncope
HP:0001645Sudden cardiac death
HP:0001663Ventricular fibrillation
HP:0001678Atrioventricular block
HP:0004308Ventricular arrhythmia

Эпидемиология (2)

Point prevalence
Unknown
Worldwide
Cases/families
Worldwide

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы