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Muenke syndrome

ORPHA:53271Malformation syndromeAutosomal dominantAntenatal, Neonatal

Ассоциированные гены (1)

FGFR3
fibroblast growth factor receptor 3
Disease-causing germline mutation(s) in
OMIM: 134934

Фенотипы (21)

Частый (30–79%)15
HP:0000248Brachycephaly
HP:0000272Malar flattening
HP:0000316Hypertelorism
HP:0000407Sensorineural hearing impairment
HP:0000508Ptosis
HP:0000520Proptosis
HP:0001357Plagiocephaly
HP:0001773Short foot
HP:0002516Increased intracranial pressure
HP:0002705High, narrow palate
HP:0004279Short palm
HP:0004440Coronal craniosynostosis
HP:0008368Tarsal synostosis
HP:0009702Carpal synostosis
HP:0010579Cone-shaped epiphysis
Периодический (5–29%)6
HP:0000238Hydrocephalus
HP:0000256Macrocephaly
HP:0001034Hypermelanotic macule
HP:0001053Hypopigmented skin patches
HP:0001263Global developmental delay
HP:0005599Hypopigmentation of hair

Эпидемиология (3)

Prevalence at birth
1-9 / 100 000
Worldwide
Point prevalence
Unknown
Worldwide
Prevalence at birth
1-9 / 100 000
Australia

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы