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Idiopathic bronchiectasis

ORPHA:60033DiseaseNot applicableAll ages

Ассоциированные гены (4)

CFTR
CF transmembrane conductance regulator
Candidate gene tested in
OMIM: 602421
SCNN1A
sodium channel epithelial 1 subunit alpha
Disease-causing germline mutation(s) in
OMIM: 600228
SCNN1B
sodium channel epithelial 1 subunit beta
Disease-causing germline mutation(s) in
OMIM: 600760
SCNN1G
sodium channel epithelial 1 subunit gamma
Disease-causing germline mutation(s) in
OMIM: 600761

Фенотипы (19)

Облигатный (100%)1
HP:0002110Bronchiectasis
Очень частый (80–99%)3
HP:0002795Abnormal respiratory system physiology
HP:0011947Respiratory tract infection
HP:0031245Productive cough
Частый (30–79%)8
HP:0002094Dyspnea
HP:0002105Hemoptysis
HP:0002783Recurrent lower respiratory tract infections
HP:0005376Recurrent Haemophilus influenzae infections
HP:0030828Wheezing
HP:0030830Crackles
HP:0030877Reduced FEV1/FVC ratio
HP:0100749Chest pain
Периодический (5–29%)6
HP:0001658Myocardial infarction
HP:0001945Fever
HP:0002097Emphysema
HP:0004326Cachexia
HP:0011949Acute infectious pneumonia
HP:0100812Halitosis
Очень редкий (1–4%)1
HP:0001217Clubbing

Эпидемиология (3)

Annual incidence
1-9 / 100 000
Finland
Prevalence at birth
1-5 / 10 000
Finland
Point prevalence
1-5 / 10 000
Europe

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы