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Autosomal dominant hereditary chronic pancreatitis

ORPHA:676DiseaseAutosomal dominantAdolescent, Childhood

Ассоциированные гены (6)

CASR
calcium sensing receptor
Candidate gene tested in
OMIM: 601199
PRSS1
serine protease 1
Disease-causing germline mutation(s) (gain of function) in
OMIM: 276000
PRSS2
serine protease 2
Candidate gene tested in
OMIM: 601564
CTRC
chymotrypsin C
Candidate gene tested in
OMIM: 601405
CPA1
carboxypeptidase A1
Major susceptibility factor in
OMIM: 114850
TRPV6
transient receptor potential cation channel subfamily V member 6
Major susceptibility factor in
OMIM: 606680

Фенотипы (9)

Очень частый (80–99%)4
HP:0001974Leukocytosis
HP:0002027Abdominal pain
HP:0011227Elevated circulating C-reactive protein concentration
HP:0100027Recurrent pancreatitis
Частый (30–79%)1
HP:0012379Abnormal enzyme/coenzyme activity
Периодический (5–29%)4
HP:0000819Diabetes mellitus
HP:0000952Jaundice
HP:0005213Pancreatic calcification
HP:0030247Splanchnic vein thrombosis

Эпидемиология (3)

Point prevalence
1-9 / 1 000 000
France
Point prevalence
1-9 / 1 000 000
Denmark
Point prevalence
1-9 / 1 000 000
Europe

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы