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Low phospholipid-associated cholelithiasis

ORPHA:69663DiseaseAutosomal dominant, Autosomal recessiveAdult

Ассоциированные гены (1)

ABCB4
ATP binding cassette subfamily B member 4
Disease-causing germline mutation(s) (loss of function) in
OMIM: 171060

Фенотипы (19)

Очень частый (80–99%)2
HP:0001406Intrahepatic cholestasis
HP:0011848Abdominal colic
Частый (30–79%)4
HP:0001081Cholelithiasis
HP:0002910Elevated circulating hepatic transaminase concentration
HP:0025502Overweight
HP:0030948Elevated gamma-glutamyltransferase level
Периодический (5–29%)9
HP:0000822Hypertension
HP:0001082Cholecystitis
HP:0001402Hepatocellular carcinoma
HP:0001513Obesity
HP:0001733Pancreatitis
HP:0002896Neoplasm of the liver
HP:0003124Hypercholesterolemia
HP:0005230Biliary tract obstruction
HP:0030151Cholangitis
Очень редкий (1–4%)4
HP:0000819Diabetes mellitus
HP:0002613Biliary cirrhosis
HP:0030991Sclerosing cholangitis
HP:0100523Liver abscess

Эпидемиология (1)

Point prevalence
Unknown
Worldwide

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы