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Cholangiocarcinoma

ORPHA:70567DiseaseNot applicableAdult

Ассоциированные гены (4)

BRCA1
BRCA1 DNA repair associated
Disease-causing somatic mutation(s) in
OMIM: 113705
BRCA2
BRCA2 DNA repair associated
Disease-causing somatic mutation(s) in
OMIM: 600185
ROS1
ROS proto-oncogene 1, receptor tyrosine kinase
Part of a fusion gene in
OMIM: 165020
PTPN3
protein tyrosine phosphatase non-receptor type 3
Disease-causing somatic mutation(s) in
OMIM: 176877

Фенотипы (8)

Очень частый (80–99%)3
HP:0000952Jaundice
HP:0011985Acholic stools
HP:0100574Biliary tract neoplasm
Частый (30–79%)2
HP:0000989Pruritus
HP:0012378Fatigue
Периодический (5–29%)3
HP:0001945Fever
HP:0002027Abdominal pain
HP:0002039Anorexia

Эпидемиология (8)

Annual incidence
1-9 / 100 000
Worldwide
Point prevalence
1-9 / 100 000
Worldwide
Annual incidence
1-9 / 100 000
United States
Annual incidence
>1 / 1000
Thailand
Annual incidence
1-9 / 100 000
Japan
Annual incidence
1-9 / 1 000 000
Australia
Annual incidence
1-9 / 100 000
Europe
Point prevalence
1-9 / 100 000
Europe

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы