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Atrophoderma vermiculata

ORPHA:79100DiseaseAutosomal recessive, UnknownChildhood

Ассоциированные гены (1)

LRP1
LDL receptor related protein 1
Disease-causing germline mutation(s) (loss of function) in
OMIM: 107770

Фенотипы (17)

Очень частый (80–99%)5
HP:0001075Atrophic scars
HP:0004426Abnormality of the cheek
HP:0007515Hypoplastic pilosebaceous units
HP:0011124Abnormality of epidermal morphology
HP:0100276Skin pit
Частый (30–79%)4
HP:0000306Abnormality of the chin
HP:0007502Follicular hyperkeratosis
HP:0045059Hyperkeratotic papule
HP:0100277Periauricular skin pits
Периодический (5–29%)8
HP:0000290Abnormality of the forehead
HP:0000464Abnormality of the neck
HP:0000708Atypical behavior
HP:0000989Pruritus
HP:0001067Neurofibromas
HP:0010783Erythema
HP:0012531Pain
HP:0012722Heart block

Эпидемиология (1)

Point prevalence
Unknown
Worldwide

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы