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Systemic-onset juvenile idiopathic arthritis

ORPHA:85414DiseaseMultigenic/multifactorial, UnknownChildhood

Ассоциированные гены (4)

HLA-DRB1
major histocompatibility complex, class II, DR beta 1
Major susceptibility factor in
OMIM: 142857
MIF
macrophage migration inhibitory factor
Major susceptibility factor in
OMIM: 153620
IL6
interleukin 6
Major susceptibility factor in
OMIM: 147620
LACC1
laccase domain containing 1
Disease-causing germline mutation(s) in
OMIM: 613409

Фенотипы (22)

Очень частый (80–99%)9
HP:0000988Skin rash
HP:0001369Arthritis
HP:0001386Joint swelling
HP:0001945Fever
HP:0002829Arthralgia
HP:0002960Autoimmunity
HP:0003565Elevated erythrocyte sedimentation rate
HP:0005681Juvenile rheumatoid arthritis
HP:0011227Elevated circulating C-reactive protein concentration
Частый (30–79%)1
HP:0002716Lymphadenopathy
Периодический (5–29%)12
HP:0000099Glomerulonephritis
HP:0000938Osteopenia
HP:0001510Growth delay
HP:0001701Pericarditis
HP:0001744Splenomegaly
HP:0002027Abdominal pain
HP:0002202Pleural effusion
HP:0002240Hepatomegaly
HP:0003281Increased circulating ferritin concentration
HP:0004890Elevated pulmonary artery pressure
HP:0012122Anterior uveitis
HP:0033430Non-infectious meningitis

Эпидемиология (2)

Point prevalence
1-9 / 100 000
Worldwide
Annual incidence
1-9 / 1 000 000
Worldwide

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы