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Acute myeloid leukaemia with myelodysplasia-related features

ORPHA:86845DiseaseNot applicableAdult

Ассоциированные гены (5)

TET2
tet methylcytosine dioxygenase 2
Disease-causing somatic mutation(s) in
OMIM: 612839
IDH1
isocitrate dehydrogenase (NADP(+)) 1
Disease-causing somatic mutation(s) in
OMIM: 147700
IDH2
isocitrate dehydrogenase (NADP(+)) 2
Disease-causing somatic mutation(s) in
OMIM: 147650
ASXL1
ASXL transcriptional regulator 1
Disease-causing somatic mutation(s) in
OMIM: 612990
DNMT3A
DNA methyltransferase 3 alpha
Disease-causing somatic mutation(s) in
OMIM: 602769

Эпидемиология (1)

Annual incidence
<1 / 1 000 000
Europe

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы