← Назад

Granulomatosis with polyangiitis

ORPHA:900DiseaseNot applicableAdolescent, Adult, Childhood, Elderly

Ассоциированные гены (5)

HLA-DPA1
major histocompatibility complex, class II, DP alpha 1
Major susceptibility factor in
OMIM: 142880
HLA-DPB1
major histocompatibility complex, class II, DP beta 1
Major susceptibility factor in
OMIM: 142858
CTLA4
cytotoxic T-lymphocyte associated protein 4
Major susceptibility factor in
OMIM: 123890
PTPN22
protein tyrosine phosphatase non-receptor type 22
Major susceptibility factor in
OMIM: 600716
PRTN3
proteinase 3
Major susceptibility factor in
OMIM: 177020

Фенотипы (80)

Очень частый (80–99%)17
HP:0000163Abnormal oral cavity morphology
HP:0000246Sinusitis
HP:0000366Abnormality of the nose
HP:0000388Otitis media
HP:0000421Epistaxis
HP:0000790Hematuria
HP:0001824Weight loss
HP:0001945Fever
HP:0002113Pulmonary infiltrates
HP:0002205Recurrent respiratory infections
HP:0002633Vasculitis
HP:0002637Cerebral ischemia
HP:0002829Arthralgia
HP:0002955Granulomatosis
HP:0002960Autoimmunity
HP:0012378Fatigue
HP:0100820Glomerulopathy
Частый (30–79%)28
HP:0000093Proteinuria
HP:0000099Glomerulonephritis
HP:0000579Nasolacrimal duct obstruction
HP:0000864Abnormality of the hypothalamus-pituitary axis
HP:0000988Skin rash
HP:0001369Arthritis
HP:0002017Nausea and vomiting
HP:0002027Abdominal pain
HP:0002093Respiratory insufficiency
HP:0002105Hemoptysis
HP:0002206Pulmonary fibrosis
HP:0003565Elevated erythrocyte sedimentation rate
HP:0005764Polyarticular arthritis
HP:0006510Chronic pulmonary obstruction
HP:0006535Recurrent intrapulmonary hemorrhage
HP:0009830Peripheral neuropathy
HP:0011227Elevated circulating C-reactive protein concentration
HP:0012649Increased inflammatory response
HP:0012735Cough
HP:0032230Cytoplasmic antineutrophil antibody positivity
HP:0033557Anti-proteinase 3 antibody positivity
HP:0033559Anti-myeloperoxidase antibody positivity
HP:0034104Anti-neutrophil elastase antibody positivity
HP:0100532Scleritis
HP:0100533Inflammatory abnormality of the eye
HP:0100539Periorbital edema
HP:0100749Chest pain
HP:0200034Papule
Периодический (5–29%)35
HP:0000024Prostatitis
HP:0000071Ureteral stenosis
HP:0000083Renal insufficiency
HP:0000126Hydronephrosis
HP:0000389Chronic otitis media
HP:0000407Sensorineural hearing impairment
HP:0000488Retinopathy
HP:0000491Keratitis
HP:0000505Visual impairment
HP:0000520Proptosis
HP:0000763Sensory neuropathy
HP:0000822Hypertension
HP:0000873Diabetes insipidus
HP:0000979Purpura
HP:0001250Seizure
HP:0001287Meningitis
HP:0001607Subglottic stenosis
HP:0001681Angina pectoris
HP:0001701Pericarditis
HP:0001733Pancreatitis
HP:0002091Restrictive ventilatory defect
HP:0002102Pleuritis
HP:0002202Pleural effusion
HP:0002239Gastrointestinal hemorrhage
HP:0002301Hemiplegia
HP:0002315Headache
HP:0003326Myalgia
HP:0004936Venous thrombosis
HP:0005214Intestinal obstruction
HP:0006824Cranial nerve paralysis
HP:0011675Arrhythmia
HP:0025420Diffuse alveolar hemorrhage
HP:0033608Pulmonary nodule
HP:0100758Gangrene
HP:0200042Skin ulcer

Эпидемиология (25)

Annual incidence
1-9 / 1 000 000
Europe
Point prevalence
1-9 / 100 000
Europe
Annual incidence
1-9 / 100 000
United Kingdom
Point prevalence
1-5 / 10 000
Sweden
Annual incidence
1-9 / 1 000 000
Germany
Point prevalence
1-9 / 100 000
France
Annual incidence
1-9 / 100 000
Sweden
Annual incidence
1-9 / 1 000 000
Spain
Point prevalence
1-9 / 100 000
Norway
Annual incidence
1-9 / 100 000
Norway
Point prevalence
1-9 / 100 000
Australia
Point prevalence
1-9 / 100 000
New Zealand
Annual incidence
1-9 / 1 000 000
Finland
Point prevalence
1-9 / 100 000
United States
Point prevalence
1-9 / 100 000
China
Annual incidence
1-9 / 1 000 000
Lithuania
Annual incidence
1-9 / 1 000 000
Greece
Annual incidence
1-9 / 1 000 000
Italy
Annual incidence
1-9 / 1 000 000
Canada
Annual incidence
1-9 / 1 000 000
Japan
Annual incidence
<1 / 1 000 000
Taiwan, Province of China
Point prevalence
1-9 / 1 000 000
Japan
Point prevalence
1-9 / 100 000
Italy
Point prevalence
1-5 / 10 000
Denmark
Annual incidence
1-9 / 100 000
United States

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы