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Early-onset nuclear cataract

ORPHA:98991Clinical subtypeAutosomal dominant, Autosomal recessive, X-linked recessiveInfancy, Neonatal

Ассоциированные гены (18)

WFS1
wolframin ER transmembrane glycoprotein
Disease-causing germline mutation(s) in
OMIM: 606201
CRYAA
crystallin alpha A
Disease-causing germline mutation(s) in
OMIM: 123580
CRYAB
crystallin alpha B
Disease-causing germline mutation(s) in
OMIM: 123590
CRYBA1
crystallin beta A1
Disease-causing germline mutation(s) in
OMIM: 123610
CRYBB2
crystallin beta B2
Disease-causing germline mutation(s) in
OMIM: 123620
CRYBB3
crystallin beta B3
Disease-causing germline mutation(s) in
OMIM: 123630
CRYGC
crystallin gamma C
Disease-causing germline mutation(s) in
OMIM: 123680
CRYGD
crystallin gamma D
Disease-causing germline mutation(s) in
OMIM: 123690
GJA3
gap junction protein alpha 3
Disease-causing germline mutation(s) in
OMIM: 121015
GJA8
gap junction protein alpha 8
Disease-causing germline mutation(s) in
OMIM: 600897
MIP
major intrinsic protein of lens fiber
Disease-causing germline mutation(s) in
OMIM: 154050
CRYBB1
crystallin beta B1
Disease-causing germline mutation(s) in
OMIM: 600929
NHS
NHS actin remodeling regulator
Disease-causing germline mutation(s) in
OMIM: 300457
BFSP1
beaded filament structural protein 1
Disease-causing germline mutation(s) in
OMIM: 603307
EPHA2
EPH receptor A2
Disease-causing germline mutation(s) in
OMIM: 176946
FYCO1
FYVE and coiled-coil domain autophagy adaptor 1
Disease-causing germline mutation(s) in
OMIM: 607182
UNC45B
unc-45 myosin chaperone B
Disease-causing germline mutation(s) in
OMIM: 611220
CRYBA2
crystallin beta A2
Disease-causing germline mutation(s) in
OMIM: 600836

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы