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Epilepsy with auditory features

ORPHA:101046DiseaseAutosomal dominantAdolescent, Adult, Childhood

Ассоциированные гены (3)

RELN
reelin
Disease-causing germline mutation(s) in
OMIM: 600514
LGI1
leucine rich glioma inactivated 1
Disease-causing germline mutation(s) (loss of function) in
OMIM: 604619
MICAL1
microtubule associated monooxygenase, calponin and LIM domain containing 1
Disease-causing germline mutation(s) in
OMIM: 607129

Фенотипы (19)

Очень частый (80–99%)3
HP:0007359Focal-onset seizure
HP:0008765Auditory hallucinations
HP:0011185EEG with focal epileptiform discharges
Частый (30–79%)2
HP:0002381Aphasia
HP:0011182Interictal epileptiform activity
Периодический (5–29%)5
HP:0002349Focal aware seizure
HP:0002367Visual hallucinations
HP:0011154Focal autonomic seizure
HP:0012332Abnormal autonomic nervous system physiology
HP:0031951Nocturnal seizures
Очень редкий (1–4%)7
HP:0000708Atypical behavior
HP:0000716Depression
HP:0002069Bilateral tonic-clonic seizure
HP:0002076Migraine
HP:0002197Generalized-onset seizure
HP:0007334Bilateral tonic-clonic seizure with focal onset
HP:0100710Impulsivity
Исключён (0%)2
HP:0001249Intellectual disability
HP:0410263Brain imaging abnormality

Эпидемиология (1)

Point prevalence
Unknown
Worldwide

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы