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Behçet disease

ORPHA:117DiseaseMultigenic/multifactorialAdolescent, Adult, Childhood

Ассоциированные гены (15)

IL10
interleukin 10
Major susceptibility factor in
OMIM: 124092
HLA-B
major histocompatibility complex, class I, B
Major susceptibility factor in
OMIM: 142830
FAS
Fas cell surface death receptor
Major susceptibility factor in
OMIM: 134637
UBAC2
UBA domain containing 2
Major susceptibility factor in
IL23R
interleukin 23 receptor
Major susceptibility factor in
OMIM: 607562
MEFV
MEFV innate immunity regulator, pyrin
Major susceptibility factor in
OMIM: 608107
STAT4
signal transducer and activator of transcription 4
Major susceptibility factor in
OMIM: 600558
C4A
complement C4A (Chido/Rodgers blood group)
Major susceptibility factor in
OMIM: 120810
IL12A
interleukin 12A
Major susceptibility factor in
OMIM: 161560
TLR4
toll like receptor 4
Major susceptibility factor in
OMIM: 603030
CCR1
C-C motif chemokine receptor 1
Major susceptibility factor in
OMIM: 601159
KLRC4
killer cell lectin like receptor C4
Major susceptibility factor in
OMIM: 602893
IL12A-AS1
IL12A antisense RNA 1
Major susceptibility factor in
ERAP1
endoplasmic reticulum aminopeptidase 1
Major susceptibility factor in
OMIM: 606832
IFNGR1
interferon gamma receptor 1
Major susceptibility factor in
OMIM: 107470

Фенотипы (85)

Очень частый (80–99%)14
HP:0000155Oral ulcer
HP:0000613Photophobia
HP:0001287Meningitis
HP:0001369Arthritis
HP:0001482Subcutaneous nodule
HP:0001945Fever
HP:0002017Nausea and vomiting
HP:0002076Migraine
HP:0002633Vasculitis
HP:0003326Myalgia
HP:0011107Recurrent aphthous stomatitis
HP:0012378Fatigue
HP:0100796Orchitis
HP:0200034Papule
Частый (30–79%)21
HP:0001061Acne
HP:0001269Hemiparesis
HP:0001288Gait disturbance
HP:0001289Confusion
HP:0002027Abdominal pain
HP:0002239Gastrointestinal hemorrhage
HP:0002315Headache
HP:0002638Superficial thrombophlebitis
HP:0002829Arthralgia
HP:0003249Genital ulcers
HP:0003565Elevated erythrocyte sedimentation rate
HP:0004936Venous thrombosis
HP:0007813Nongranulomatous uveitis
HP:0008066Abnormal blistering of the skin
HP:0011227Elevated circulating C-reactive protein concentration
HP:0012121Panuveitis
HP:0012219Erythema nodosum
HP:0012649Increased inflammatory response
HP:0025532Positive pathergy test
HP:0100326Immunologic hypersensitivity
HP:0200039Pustule
Периодический (5–29%)48
HP:0002024Malabsorption
HP:0002039Anorexia
HP:0002102Pleuritis
HP:0002105Hemoptysis
HP:0002113Pulmonary infiltrates
HP:0002202Pleural effusion
HP:0002204Pulmonary embolism
HP:0002321Vertigo
HP:0002354Memory impairment
HP:0002376Developmental regression
HP:0002383Infectious encephalitis
HP:0002516Increased intracranial pressure
HP:0002637Cerebral ischemia
HP:0002716Lymphadenopathy
HP:0003401Paresthesia
HP:0004420Arterial thrombosis
HP:0006824Cranial nerve paralysis
HP:0007256Abnormal pyramidal sign
HP:0010885Avascular necrosis
HP:0012819Myocarditis
HP:0033430Non-infectious meningitis
HP:0000031Epididymitis
HP:0000083Renal insufficiency
HP:0000488Retinopathy
HP:0000518Cataract
HP:0000618Blindness
HP:0000708Atypical behavior
HP:0000737Irritability
HP:0001097Keratoconjunctivitis sicca
HP:0001250Seizure
HP:0001251Ataxia
HP:0001347Hyperreflexia
HP:0001637Abnormal myocardium morphology
HP:0001653Mitral regurgitation
HP:0001658Myocardial infarction
HP:0001659Aortic regurgitation
HP:0001701Pericarditis
HP:0001733Pancreatitis
HP:0001744Splenomegaly
HP:0001824Weight loss
HP:0001954Recurrent fever
HP:0100584Endocarditis
HP:0100614Myositis
HP:0100653Optic neuritis
HP:0100654Retrobulbar optic neuritis
HP:0100758Gangrene
HP:0100820Glomerulopathy
HP:4000041AA amyloidosis
Очень редкий (1–4%)2
HP:0000099Glomerulonephritis
HP:0002014Diarrhea

Эпидемиология (18)

Annual incidence
1-9 / 1 000 000
Spain
Annual incidence
1-9 / 1 000 000
Italy
Point prevalence
1-9 / 100 000
United States
Annual incidence
1-9 / 1 000 000
Iran, Islamic Republic of
Point prevalence
1-9 / 100 000
France
Point prevalence
1-9 / 100 000
Italy
Point prevalence
1-5 / 10 000
United Kingdom
Point prevalence
1-9 / 100 000
Sweden
Point prevalence
1-9 / 100 000
Portugal
Point prevalence
1-5 / 10 000
Japan
Point prevalence
>1 / 1000
Turkey
Point prevalence
1-5 / 10 000
Iran, Islamic Republic of
Point prevalence
1-5 / 10 000
Israel
Point prevalence
1-9 / 100 000
Taiwan, Province of China
Annual incidence
1-9 / 1 000 000
Taiwan, Province of China
Point prevalence
1-5 / 10 000
Saudi Arabia
Point prevalence
1-9 / 100 000
Europe
Annual incidence
1-9 / 100 000
Korea, Republic of

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы