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Isolated cleft lip

ORPHA:199302Morphological anomalyMultigenic/multifactorialInfancy, Neonatal

Ассоциированные гены (4)

TP63
tumor protein p63
Major susceptibility factor in
OMIM: 603273
IRF6
interferon regulatory factor 6
Major susceptibility factor in
OMIM: 607199
NECTIN1
nectin cell adhesion molecule 1
Major susceptibility factor in
OMIM: 600644
MSX1
msh homeobox 1
Major susceptibility factor in
OMIM: 142983

Фенотипы (19)

Частый (30–79%)2
HP:0000389Chronic otitis media
HP:0100335Non-midline cleft of the upper lip
Периодический (5–29%)10
HP:0000220Velopharyngeal insufficiency
HP:0000708Atypical behavior
HP:0001518Small for gestational age
HP:0001572Macrodontia
HP:0006332Supernumerary maxillary incisor
HP:0009088Speech articulation difficulties
HP:0011438Maternal teratogenic exposure
HP:0031469Low self esteem
HP:0040115Abnormality of the Eustachian tube
HP:0100336Bilateral cleft lip
Очень редкий (1–4%)7
HP:0000405Conductive hearing impairment
HP:0000668Hypodontia
HP:0001328Specific learning disability
HP:0001537Umbilical hernia
HP:0001561Polyhydramnios
HP:0001696Situs inversus totalis
HP:0001762Talipes equinovarus

Эпидемиология (1)

Point prevalence
1-5 / 10 000
Europe

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы