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Congenital stationary night blindness

ORPHA:215Clinical groupAutosomal dominant, Autosomal recessive, X-linked recessiveNeonatal

Ассоциированные гены (1)

RHO
rhodopsin
Disease-causing germline mutation(s) in
OMIM: 180380

Фенотипы (15)

Очень частый (80–99%)4
HP:0000545Myopia
HP:0000662Nyctalopia
HP:0007663Reduced visual acuity
HP:0030469Abnormal dark-adapted electroretinogram
Частый (30–79%)4
HP:0000486Strabismus
HP:0000639Nystagmus
HP:0030638Congenital stationary night blindness with normal fundus
HP:0030639Congenital stationary night blindness with abnormal fundus
Периодический (5–29%)4
HP:0000540Hypermetropia
HP:0007984Electronegative electroretinogram
HP:0030483Reduced amplitude of dark-adapted bright flash electroretinogram a-wave
HP:0031705Compensatory head posture
Очень редкий (1–4%)3
HP:0000551Color vision defect
HP:0007703Abnormality of retinal pigmentation
HP:0030329Retinal thinning

Эпидемиология (1)

Point prevalence
Unknown
Worldwide

Лекарства и терапия

Источник: Open Targets Platform (в реальном времени)

Клинические исследования

Источник: ClinicalTrials.gov (в реальном времени)

Внешние ресурсы